Comparing real-world evidence usage in gene therapy health technology assessments: Implications for achieving alignment in future joint clinical assessments

<b>Background &amp; Objective</b>: The unprecedented value and long­term uncertainties of gene therapies have challenged established health technology assessment (HTA) methods. Real-world data (RWD) and real-world evidence (RWE) may mitigate the encountered uncertainties. However, empirical evidence appears to be lacking in the literature. This...